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Leslie Matalonga Selected Research

Lysergic Acid Diethylamide (LSD)

9/2012Discovery of a novel noniminosugar acid α glucosidase chaperone series.

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Leslie Matalonga Research Topics

Disease

2Congenital Myasthenic Syndromes (Myasthenia Gravis, Congenital)
03/2024 - 09/2023
2Intellectual Disability (Idiocy)
01/2023 - 01/2021
1Muscular Diseases (Myopathy)
03/2024
1Disease Progression
03/2023
1Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)
03/2023
1Autistic Disorder (Autism)
01/2023
1Metabolic Diseases (Metabolic Disease)
01/2022
1Focal Dermal Hypoplasia (Syndrome, Goltz)
02/2021
1Muscle Spasticity (Spastic)
01/2021
1Headache (Headaches)
01/2021
1Epilepsy (Aura)
01/2021
1Vomiting
01/2021
1Neoplasms (Cancer)
01/2021
1Rare Diseases (Rare Disease)
12/2020
1Congenital Disorders of Glycosylation
01/2017
1Parkinsonian Disorders (Parkinsonism)
01/2017
1Mucopolysaccharidosis III (Sanfilippo Syndrome)
05/2014
1Lactic Acidosis
04/2014
1Brain Diseases (Brain Disorder)
09/2013
1Teratoma (Teratoid Tumor)
02/2013
1Gaucher Disease (Gaucher's Disease)
02/2013
1Glycogen Storage Disease Type II (Pompe's Disease)
09/2012

Drug/Important Bio-Agent (IBA)

3Proteins (Proteins, Gene)FDA Link
01/2022 - 01/2017
2Thioctic Acid (Lipoic Acid)IBA
04/2014 - 09/2013
2EnzymesIBA
02/2013 - 09/2012
2AcidsIBA
02/2013 - 09/2012
2GlucosidasesIBA
02/2013 - 09/2012
1DesminIBA
03/2024
1muskIBA
09/2023
1Cholinesterase Inhibitors (Anticholinesterases)IBA
09/2023
1Adrenergic Agonists (Adrenergic Receptor Agonist)IBA
09/2023
1DystrophinIBA
03/2023
1NucleotidesIBA
01/2023
1Proline (L-Proline)FDA Link
02/2021
1Nonsense Codon (Nonsense Mutation)IBA
02/2021
1Mitochondrial DNA (mtDNA)IBA
01/2021
1DNA (Deoxyribonucleic Acid)IBA
01/2021
1Complement System Proteins (Complement)IBA
12/2020
1LipidsIBA
01/2017
1Protons (Proton)IBA
05/2014
1HydrolasesIBA
05/2014
1AntioxidantsIBA
05/2014
1coenzyme Q10 (CoQ10)IBA
05/2014
1Ketoglutaric Acids (Ketoglutaric Acid)IBA
04/2014
1Pyruvic Acid (Pyruvate)IBA
04/2014
1Oxidoreductases (Dehydrogenase)IBA
04/2014
1SphingolipidsIBA
02/2013
1Lysergic Acid Diethylamide (LSD)IBA
09/2012

Therapy/Procedure

1Treatment Delay
12/2020
1Therapeutics
12/2020
1Enzyme Replacement Therapy
09/2012